What is gene therapy?

Gene therapy aims to treat the genetic disorders by replacing or inactivating genes or introducing corrective genes into cells1

Find out more about gene therapy and the future on AADC deficiency management:

References: 1. American Society of Gene and Cell Therapy. Available at: https://patienteducation.asgct.org/gene-therapy-101/gene-therapybasics.Last accessed October 2021

AE-AADC-0267 | August 2022