What is gene therapy – PTC

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What is gene therapy?

Gene therapy aims to treat the genetic disorders by replacing or inactivating genes or introducing corrective genes into cells¹

Find out more about gene therapy and the future on AADC deficiency management:

References: 1. American Society of Gene and Cell Therapy. Available at: https://patienteducation.asgct.org/gene-therapy-101/gene-therapybasics.Last accessed October 2021

AE-AADC-0267 | August 2022

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